BioMarin External Research Program

About this program

BioMarin’s External Research Program provides funding and/or investigational product for investigator‑sponsored clinical research that advances understanding of BioMarin medicines, product candidates, or disease areas of interest, supporting interventional studies (Phase 1–4), observational studies, real‑world evidence projects, and product‑only requests. The program excludes non‑clinical/animal research, continuing medical education or non‑CME education, event sponsorships, and charitable contributions; applicants must contact their regional BioMarin representative and request an external research application pack before submission. Applications must include a proposal form (background, objectives, endpoints, inclusion/exclusion criteria, population and sample size), a funding/product form with an itemized, institution‑approved budget, a current CV, and contracting institution information; review typically takes four to eight weeks. Budgets must not include standard‑of‑care costs or poorly defined items, and overhead above 30% requires supporting institutional documentation, so ensure institutional contracting and budget approvals in advance.